An effort is ongoing to collect valentines for Massillon resident Vinny DeMando, 7, who has muscular dystrophy. Cards are ...
Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...
Evan McMenamin said his brother Travis, "never lets it get him down" despite the "incredible challenges" he faces ...
Roche has announced positive results from the Phase III EMBARK clinical trial of Elevidys (delandistrogene moxeparvovec) for the treatment of Duchenne muscular dystrophy (DMD ... “As Duchenne ...
has granted Fast Track designation for DYNE-101 for the treatment of myotonic dystrophy type 1 (DM1). DYNE-101 is currently being evaluated in the ongoing Phase 1/2 ACHIEVE global clinical trial.
The evidence surrounding the use of puberty blockers and cross sex hormones in children and teens identifying ... and caregivers,” they wrote. “Treatment decisions should consider the lack ...
The U.S. Food and Drug Administration (FDA) has granted fast track designation to DYNE-101, a treatment candidate for myotonic ... one of two types of myotonic dystrophy — the most common form of ...
The FDA has granted fast-track designation to an investigational antisense oligonucleotide to treat individuals with myotonic dystrophy type ... Agency for the treatment of DM1, a monogenic ...
There is no cure for spinal muscular atrophy, but treatments can stop its progression and often lead to some improvement. However, Manitoba has refused to pay for the hugely expensive treatment ...
DYNE-101 has been granted orphan drug designation by the U.S. Food and Drug Administration and the European Medicines Agency for the treatment ... dystrophy type 1 (DM1) and Duchenne muscular ...
When children with obesity undergo weight-loss treatment, the results have effects later in life, and the risk of serious health problems and premature death is lower as they reach young adulthood.
The treatment studied involved support for children with obesity and their families designed to motivate healthy diets, exercise and sleep habits -- what is known as "behavioural lifestyle therapy." ...