About Evrysdi Evrysdi is an SMN2-splicing modifier designed to increase functional SMN protein production. With the introduction of a new tablet formulation, Evrysdi now offers an alternative ...
Managed Healthcare Executive provides C-suite executives at health plans and provider organizations with news, analysis, ...
Utrophin increase in muscle cells after transcriptional adaptation normalises cell function in Duchenne muscular ...
These names in the biotech sector are seeing a substantial increase in search activity today, as determined by InvestingChannel. They ...
"Preserving Public Trust in U.S. Newborn Screening System," authored by NORD in partnership with a dozen rare disease patient advocacy organizations, explores the retention and se ...
Blizzard Entertainment and World of Warcraft players raised over $2 million for CureDuchenne, honoring Mats Steen, a devoted player lost to Duchenne muscular dystrophy, while promoting awareness and ...
A self-confessed nerd, Vijay Iyer went high-tech to learn a few new dance moves. The SNOLAB physicist — he is currently ...
U.S. Sen. Susan Collins said she also opposes "the poorly conceived conceived directive" from the National Institutes for ...
A federal judge in Boston granted on Monday a temporary restraining order sought by Maine Attorney General Aaron Frey and ...
Senate Appropriations Committee ranking member Patty Murray, D-Wash., wrote in a statement the NIH policy change amounts to ...