The Muscular Dystrophy Association celebrates this new more accessible treatment option for people living with SMA. MDA - New ...
A scheduled charity wrestling event in August will bring a famous name from pro wrestling, who's also a former gold medalist, ...
US biotech Abcuro has reeled in $200 million in third-round financing that should allow it to complete its pivotal trial of ...
Over the past nine years, patients with spinal muscular atrophy have seen the number of FDA-approved treatment options for ...
The University of Rochester will confront significant blows to groundbreaking clinical studies, UR says in a legal challenge to cuts in NIH funding.
Zacks Small Cap Research on MSN3h
ARWR: Multiple Catalysts Ahead in 2025…
Part 1 of the trial will assess single and multiple doses of ARO-INHBE monotherapy, while Part 2 of the study will assess ARO-INHBE in combination with tirzepatide. We anticipate results from Part 1 ...
Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...
The 5 mg risdiplam tablet provides the same efficacy and safety for spinal muscular atrophy as the currently available oral ...